Authors
Lab
Journal
bioRxiv
Abstract
Antisense therapeutics such as splice-modulating antisense oligonucleotides (ASOs) are promising tools to treat diseases caused by splice-altering intronic variants. However, their
Keywords/Topics
Humanized mouse model ; Collagen VI - related muscular dystrophies ;COL6A1 ; pseudoexon Introduction Collagen VI - related
BIOSEB Instruments Used:
Grip strength test (BIO-GS4)
Source :
Congrès & Meetings 2026 