Authors
Cossins, Judith, Kozma, Imre, Canzonetta, Claudia, Hawkins, Al, Beeson, David, Sepulveda, Patricio, Dong, Yin Yao
Lab
Journal
Brain Communications
Abstract
Cossins et al. show that a novel adeno-associated viral gene therapy rescues a severe mouse model of DOK7 congenital myasthenia, making them as strong as w
Keywords/Topics
congenital myasthenia; gene therapy; DOK7-AAV; pre-clinical trial; neuromuscular junction
BIOSEB Instruments Used:
Grip strength test (BIO-GS4)
Source :
https://academic.oup.com/braincomms/article-abstract/7/1/fcaf046/7990910
CONFERENCES & MEETINGS 